Sequence-dependent cytotoxicity of second-generation oligonucleotides

od Drygin, Denis, Barone, Stephen, Bennett, C. Frank
Wydane 2004

Selective tissue targeting of synthetic nucleic acid drugs

od Seth, Punit P., Tanowitz, Michael, Bennett, C. Frank
Wydane w J Clin Invest (2019)

RNase H-mediated degradation of toxic RNA in myotonic dystrophy type 1

od Lee, Johanna E., Bennett, C. Frank, Cooper, Thomas A.
Wydane 2012

Antisense Oligonucleotide Therapies for Neurodegenerative Diseases

od Bennett, C. Frank, Krainer, Adrian R., Cleveland, Don W.
Wydane w Annu Rev Neurosci (2019)

Antisense-based therapy for the treatment of spinal muscular atrophy

od Rigo, Frank, Hua, Yimin, Krainer, Adrian R., Bennett, C. Frank
Wydane 2012

Phosphorothioate Antisense Oligonucleotides Induce the Formation of Nuclear Bodies

od Lorenz, Peter, Baker, Brenda F., Bennett, C. Frank, Spector, David L.
Wydane 1998

Nonsense-mediated decay as a terminating mechanism for antisense oligonucleotides

od Ward, Amanda J., Norrbom, Michaela, Chun, Seung, Bennett, C. Frank, Rigo, Frank
Wydane 2014

Delivery of GalNAc-Conjugated Splice-Switching ASOs to Non-hepatic Cells through Ectopic Expression of Asialoglycoprotein Receptor

od Scharner, Juergen, Qi, Sabrina, Rigo, Frank, Bennett, C. Frank, Krainer, Adrian R.
Wydane w Mol Ther Nucleic Acids (2019)

Comparison of the efficacy of MOE and PMO modifications of systemic antisense oligonucleotides in a severe SMA mouse model

od Sheng, Lei, Rigo, Frank, Bennett, C Frank, Krainer, Adrian R, Hua, Yimin
Wydane w Nucleic Acids Res (2020)

Nucleocytoplasmic shuttling: a novel in vivo property of antisense phosphorothioate oligodeoxynucleotides

od Lorenz, Peter, Misteli, Tom, Baker, Brenda F., Bennett, C. Frank, Spector, David L.
Wydane 2000

Manipulation of PK-M mutually exclusive alternative splicing by antisense oligonucleotides

od Wang, Zhenxun, Jeon, Hyun Yong, Rigo, Frank, Bennett, C. Frank, Krainer, Adrian R.
Wydane 2012

Systemic therapy in an RNA toxicity mouse model with an antisense oligonucleotide therapy targeting a non-CUG sequence within the DMPK 3′UTR RNA

od Yadava, Ramesh S, Yu, Qing, Mandal, Mahua, Rigo, Frank, Bennett, C Frank, Mahadevan, Mani S
Wydane w Hum Mol Genet (2020)

Fully modified 2′ MOE oligonucleotides redirect polyadenylation

od Vickers, Timothy A., Wyatt, Jacqueline R., Burckin, Todd, Bennett, C. Frank, Freier, Susan M.
Wydane 2001

Enhancement of SMN2 Exon 7 Inclusion by Antisense Oligonucleotides Targeting the Exon

od Hua, Yimin, Vickers, Timothy A, Baker, Brenda F, Bennett, C. Frank, Krainer, Adrian R
Wydane 2007

Antisense Masking of an hnRNP A1/A2 Intronic Splicing Silencer Corrects SMN2 Splicing in Transgenic Mice

od Hua, Yimin, Vickers, Timothy A., Okunola, Hazeem L., Bennett, C. Frank, Krainer, Adrian R.
Wydane 2008

Mechanisms of single-stranded phosphorothioate modified antisense oligonucleotide accumulation in hepatocytes

od Koller, Erich, Vincent, Thomas M., Chappell, Alfred, De, Soma, Manoharan, Muthiah, Bennett, C. Frank
Wydane 2011

Widespread recognition of 5′ splice sites by noncanonical base-pairing to U1 snRNA involving bulged nucleotides

od Roca, Xavier, Akerman, Martin, Gaus, Hans, Berdeja, Andrés, Bennett, C. Frank, Krainer, Adrian R.
Wydane 2012

Modeling muscle regeneration in RNA toxicity mice

od Yadava, Ramesh S, Mandal, Mahua, Giese, Jack M, Rigo, Frank, Bennett, C Frank, Mahadevan, Mani S
Wydane w Hum Mol Genet (2021)

Motor neuron cell-nonautonomous rescue of spinal muscular atrophy phenotypes in mild and severe transgenic mouse models

od Hua, Yimin, Liu, Ying Hsiu, Sahashi, Kentaro, Rigo, Frank, Bennett, C. Frank, Krainer, Adrian R.
Wydane w Genes Dev (2015)

Towards a therapy for Angelman syndrome by reduction of a long non-coding RNA

od Meng, Linyan, Ward, Amanda J., Chun, Seung, Bennett, C. Frank, Beaudet, Arthur L., Rigo, Frank
Wydane w Nature (2014)