Novel compounds for the treatment of Duchenne muscular dystrophy: emerging therapeutic agents

Por Wilton, Steve D, Fletcher, Sue
Publicado em 2011

Untranslated gene regions and other non-coding elements regulation of eukaryotic gene expression /

Por Barrett, Lucy W., Fletcher, Sue., Wilton, Steve D.
Publicado em 2013

Regulation of eukaryotic gene expression by the untranslated gene regions and other non-coding elements

Por Barrett, Lucy W., Fletcher, Sue, Wilton, Steve D.
Publicado em 2012

Proteomic profiling of antisense-induced exon skipping reveals reversal of pathobiochemical abnormalities in dystrophic mdx diaphragm

Por Doran, Philip, Wilton, Steve D., Fletcher, Sue, Ohlendieck, Kay
Publicado em 2009

Targeted Exon Skipping to Correct Exon Duplications in the Dystrophin Gene

Por Greer, Kane L, Lochmüller, Hanns, Flanigan, Kevin, Fletcher, Susan, Wilton, Steve D
Publicado em 2014

Evaluation of exon-skipping strategies for Duchenne muscular dystrophy utilizing dystrophin-deficient zebrafish

Por Berger, Joachim, Berger, Silke, Jacoby, Arie S, Wilton, Steve D, Currie, Peter D
Publicado no J Cell Mol Med (2011)

Molecular Diagnosis of Duchenne Muscular Dystrophy: Past, Present and Future in Relation to Implementing Therapies

Por Laing, Nigel G, Davis, Mark R, Bayley, Klair, Fletcher, Sue, Wilton, Steve D
Publicado em 2011

Translational Regulation of Utrophin by miRNAs

Por Basu, Utpal, Lozynska, Olga, Moorwood, Catherine, Patel, Gopal, Wilton, Steve D., Khurana, Tejvir S.
Publicado em 2011

Personalized exon skipping strategies to address clustered non-deletion dystrophin mutations

Por Forrest, Sarah, Meloni, Penny L, Muntoni, Francesco, Kim, Jihee, Fletcher, Sue, Wilton, Steve D
Publicado em 2010

Rational Design of Antisense Oligomers to Induce Dystrophin Exon Skipping

Por Mitrpant, Chalermchai, Adams, Abbie M, Meloni, Penny L, Muntoni, Francesco, Fletcher, Sue, Wilton, Steve D
Publicado em 2009

Mismatched single stranded antisense oligonucleotides can induce efficient dystrophin splice switching

Por Fragall, Clayton T, Adams, Abbie M, Johnsen, Russell D, Kole, Ryszard, Fletcher, Sue, Wilton, Steve D
Publicado em 2011

Antisense oligonucleotide induced exon skipping and the dystrophin gene transcript: cocktails and chemistries

Por Adams, Abbie M, Harding, Penny L, Iversen, Patrick L, Coleman, Catherine, Fletcher, Sue, Wilton, Steve D
Publicado em 2007

Prevention of Dystrophic Pathology in Severely Affected Dystrophin/Utrophin-deficient Mice by Morpholino-oligomer-mediated Exon-skipping

Por Goyenvalle, Aurélie, Babbs, Arran, Powell, Dave, Kole, Ryszard, Fletcher, Sue, Wilton, Steve D, Davies, Kay E
Publicado em 2009

Dystrophin Isoform Induction In Vivo by Antisense-mediated Alternative Splicing

Por Fletcher, Sue, Adams, Abbie M, Johnsen, Russell D, Greer, Kane, Moulton, Hong M, Wilton, Steve D
Publicado em 2010

Multiple exon skipping strategies to by-pass dystrophin mutations

Por Adkin, Carl F., Meloni, Penelope L., Fletcher, Susan, Adams, Abbie M., Muntoni, Francesco, Wong, Brenda, Wilton, Steve D.
Publicado em 2012

Improved Antisense Oligonucleotide Design to Suppress Aberrant SMN2 Gene Transcript Processing: Towards a Treatment for Spinal Muscular Atrophy

Por Mitrpant, Chalermchai, Porensky, Paul, Zhou, Haiyan, Price, Loren, Muntoni, Francesco, Fletcher, Sue, Wilton, Steve D., Burghes, Arthur H. M.
Publicado em 2013

Investigation of splicing changes and post-translational processing of LMNA in sporadic inclusion body myositis

Por Luo, Yue-Bei, Mitrpant, Chalermchai, Johnsen, Russell, Fabian, Vicki, Needham, Merrilee, Fletcher, Sue, Wilton, Steve D, Mastaglia, Frank L
Publicado em 2013

Investigation of age-related changes in LMNA splicing and expression of progerin in human skeletal muscles

Por Luo, Yue-Bei, Mitrpant, Chalermchai, Johnsen, Russell D, Fabian, Victoria A, Fletcher, Sue, Mastaglia, Frank L, Wilton, Steve D
Publicado em 2013

Antisense Oligonucleotide Induction of Progerin in Human Myogenic Cells

Por Luo, Yue-Bei, Mitrpant, Chalermchai, Adams, Abbie M., Johnsen, Russell D., Fletcher, Sue, Mastaglia, Frank L., Wilton, Steve D.
Publicado em 2014

The FSHD Atrophic Myotube Phenotype Is Caused by DUX4 Expression

Por Vanderplanck, Céline, Ansseau, Eugénie, Charron, Sébastien, Stricwant, Nadia, Tassin, Alexandra, Laoudj-Chenivesse, Dalila, Wilton, Steve D., Coppée, Frédérique, Belayew, Alexandra
Publicado em 2011