Rational Design of Antisense Oligomers to Induce Dystrophin Exon Skipping

Por Mitrpant, Chalermchai, Adams, Abbie M, Meloni, Penny L, Muntoni, Francesco, Fletcher, Sue, Wilton, Steve D
Publicado em 2009

Improved Antisense Oligonucleotide Design to Suppress Aberrant SMN2 Gene Transcript Processing: Towards a Treatment for Spinal Muscular Atrophy

Por Mitrpant, Chalermchai, Porensky, Paul, Zhou, Haiyan, Price, Loren, Muntoni, Francesco, Fletcher, Sue, Wilton, Steve D., Burghes, Arthur H. M.
Publicado em 2013

Investigation of splicing changes and post-translational processing of LMNA in sporadic inclusion body myositis

Por Luo, Yue-Bei, Mitrpant, Chalermchai, Johnsen, Russell, Fabian, Vicki, Needham, Merrilee, Fletcher, Sue, Wilton, Steve D, Mastaglia, Frank L
Publicado em 2013

Investigation of age-related changes in LMNA splicing and expression of progerin in human skeletal muscles

Por Luo, Yue-Bei, Mitrpant, Chalermchai, Johnsen, Russell D, Fabian, Victoria A, Fletcher, Sue, Mastaglia, Frank L, Wilton, Steve D
Publicado em 2013

Antisense Oligonucleotide Induction of Progerin in Human Myogenic Cells

Por Luo, Yue-Bei, Mitrpant, Chalermchai, Adams, Abbie M., Johnsen, Russell D., Fletcher, Sue, Mastaglia, Frank L., Wilton, Steve D.
Publicado em 2014

A Novel Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe Spinal Muscular Atrophy Transgenic Mice

Por Zhou, Haiyan, Janghra, Narinder, Mitrpant, Chalermchai, Dickinson, Rachel L., Anthony, Karen, Price, Loren, Eperon, Ian C., Wilton, Stephen D., Morgan, Jennifer, Muntoni, Francesco
Publicado em 2013

A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in mouse

Por Porensky, Paul N., Mitrpant, Chalermchai, McGovern, Vicki L., Bevan, Adam K., Foust, Kevin D., Kaspar, Brain K., Wilton, Stephen D., Burghes, Arthur H.M.
Publicado em 2012