Novel compounds for the treatment of Duchenne muscular dystrophy: emerging therapeutic agents

Por Wilton, Steve D, Fletcher, Sue
Publicado em 2011

Untranslated gene regions and other non-coding elements regulation of eukaryotic gene expression /

Por Barrett, Lucy W., Fletcher, Sue., Wilton, Steve D.
Publicado em 2013

Regulation of eukaryotic gene expression by the untranslated gene regions and other non-coding elements

Por Barrett, Lucy W., Fletcher, Sue, Wilton, Steve D.
Publicado em 2012

Proteomic profiling of antisense-induced exon skipping reveals reversal of pathobiochemical abnormalities in dystrophic mdx diaphragm

Por Doran, Philip, Wilton, Steve D., Fletcher, Sue, Ohlendieck, Kay
Publicado em 2009

Molecular Diagnosis of Duchenne Muscular Dystrophy: Past, Present and Future in Relation to Implementing Therapies

Por Laing, Nigel G, Davis, Mark R, Bayley, Klair, Fletcher, Sue, Wilton, Steve D
Publicado em 2011

Personalized exon skipping strategies to address clustered non-deletion dystrophin mutations

Por Forrest, Sarah, Meloni, Penny L, Muntoni, Francesco, Kim, Jihee, Fletcher, Sue, Wilton, Steve D
Publicado em 2010

Rational Design of Antisense Oligomers to Induce Dystrophin Exon Skipping

Por Mitrpant, Chalermchai, Adams, Abbie M, Meloni, Penny L, Muntoni, Francesco, Fletcher, Sue, Wilton, Steve D
Publicado em 2009

Mismatched single stranded antisense oligonucleotides can induce efficient dystrophin splice switching

Por Fragall, Clayton T, Adams, Abbie M, Johnsen, Russell D, Kole, Ryszard, Fletcher, Sue, Wilton, Steve D
Publicado em 2011

Antisense oligonucleotide induced exon skipping and the dystrophin gene transcript: cocktails and chemistries

Por Adams, Abbie M, Harding, Penny L, Iversen, Patrick L, Coleman, Catherine, Fletcher, Sue, Wilton, Steve D
Publicado em 2007

Prevention of Dystrophic Pathology in Severely Affected Dystrophin/Utrophin-deficient Mice by Morpholino-oligomer-mediated Exon-skipping

Por Goyenvalle, Aurélie, Babbs, Arran, Powell, Dave, Kole, Ryszard, Fletcher, Sue, Wilton, Steve D, Davies, Kay E
Publicado em 2009

Dystrophin Isoform Induction In Vivo by Antisense-mediated Alternative Splicing

Por Fletcher, Sue, Adams, Abbie M, Johnsen, Russell D, Greer, Kane, Moulton, Hong M, Wilton, Steve D
Publicado em 2010

Antisense suppression of donor splice site mutations in the dystrophin gene transcript

Por Fletcher, Sue, Meloni, Penny L, Johnsen, Russell D, Wong, Brenda L, Muntoni, Francesco, Wilton, Stephen D
Publicado em 2013

Improved Antisense Oligonucleotide Design to Suppress Aberrant SMN2 Gene Transcript Processing: Towards a Treatment for Spinal Muscular Atrophy

Por Mitrpant, Chalermchai, Porensky, Paul, Zhou, Haiyan, Price, Loren, Muntoni, Francesco, Fletcher, Sue, Wilton, Steve D., Burghes, Arthur H. M.
Publicado em 2013

Investigation of splicing changes and post-translational processing of LMNA in sporadic inclusion body myositis

Por Luo, Yue-Bei, Mitrpant, Chalermchai, Johnsen, Russell, Fabian, Vicki, Needham, Merrilee, Fletcher, Sue, Wilton, Steve D, Mastaglia, Frank L
Publicado em 2013

Investigation of age-related changes in LMNA splicing and expression of progerin in human skeletal muscles

Por Luo, Yue-Bei, Mitrpant, Chalermchai, Johnsen, Russell D, Fabian, Victoria A, Fletcher, Sue, Mastaglia, Frank L, Wilton, Steve D
Publicado em 2013

Antisense Oligonucleotide Induction of Progerin in Human Myogenic Cells

Por Luo, Yue-Bei, Mitrpant, Chalermchai, Adams, Abbie M., Johnsen, Russell D., Fletcher, Sue, Mastaglia, Frank L., Wilton, Steve D.
Publicado em 2014

Revertant Fibers in the mdx Murine Model of Duchenne Muscular Dystrophy: An Age- and Muscle-Related Reappraisal

Por Pigozzo, Sarah R., Da Re, Lorena, Romualdi, Chiara, Mazzara, Pietro G., Galletta, Eva, Fletcher, Sue, Wilton, Stephen D., Vitiello, Libero
Publicado em 2013

Primary over-expression of AβPP in muscle does not lead to the development of inclusion body myositis in a new lineage of the MCK-AβPP transgenic mouse

Por Luo, Yue-Bei, Johnsen, Russell D, Griffiths, Lisa, Needham, Merrilee, Fabian, Victoria A, Fletcher, Sue, Wilton, Steve D, Mastaglia, Frank L
Publicado em 2013

Targeted Exon Skipping to Address “Leaky” Mutations in the Dystrophin Gene

Por Fletcher, Sue, Adkin, Carl F., Meloni, Penny, Wong, Brenda, Muntoni, Francesco, Kole, Ryszard, Fragall, Clayton, Greer, Kane, Johnsen, Russell, Wilton, Steve D.
Publicado em 2012

Antisense-induced exon skipping and synthesis of dystrophin in the mdx mouse

Por Mann, Christopher J., Honeyman, Kaite, Cheng, Andy J., Ly, Tina, Lloyd, Frances, Fletcher, Sue, Morgan, Jennifer E., Partridge, Terry A., Wilton, Stephen D.
Publicado em 2001