In vivo dynamics of human hematopoietic stem cells: novel concepts and future directions

অনুযায়ী Scala, Serena, Aiuti, Alessandro
প্রকাশিত Blood Adv (2019)

Clinical Applications of Gene Therapy for Primary Immunodeficiencies

অনুযায়ী Cicalese, Maria Pia, Aiuti, Alessandro
প্রকাশিত Hum Gene Ther (2015)

Retroviral Integrations in Gene Therapy Trials

অনুযায়ী Biasco, Luca, Baricordi, Cristina, Aiuti, Alessandro
প্রকাশিত 2012

Gene therapy for ADA‐SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products

অনুযায়ী Aiuti, Alessandro, Roncarolo, Maria Grazia, Naldini, Luigi
প্রকাশিত EMBO Mol Med (2017)

Autologous Stem-Cell-Based Gene Therapy for Inherited Disorders: State of the Art and Perspectives

অনুযায়ী Staal, Frank J. T., Aiuti, Alessandro, Cavazzana, Marina
প্রকাশিত Front Pediatr (2019)

Update on Clinical Ex Vivo Hematopoietic Stem Cell Gene Therapy for Inherited Monogenic Diseases

অনুযায়ী Tucci, Francesca, Scaramuzza, Samantha, Aiuti, Alessandro, Mortellaro, Alessandra
প্রকাশিত Mol Ther (2021)

Autoimmune Dysregulation and Purine Metabolism in Adenosine Deaminase Deficiency

অনুযায়ী Sauer, Aisha Vanessa, Brigida, Immacolata, Carriglio, Nicola, Aiuti, Alessandro
প্রকাশিত 2012

Gene Therapy for Wiskott-Aldrich Syndrome: History, New Vectors, Future Directions

অনুযায়ী Ferrua, Francesca, Marangoni, Francesco, Aiuti, Alessandro, Roncarolo, Maria Grazia
প্রকাশিত J Allergy Clin Immunol (2020)

Gene therapy for lysosomal storage disorders: recent advances for metachromatic leukodystrophy and mucopolysaccaridosis I

অনুযায়ী Penati, Rachele, Fumagalli, Francesca, Calbi, Valeria, Bernardo, Maria Ester, Aiuti, Alessandro
প্রকাশিত J Inherit Metab Dis (2017)

How I treat ADA deficiency

অনুযায়ী Gaspar, H. Bobby, Aiuti, Alessandro, Porta, Fulvio, Candotti, Fabio, Hershfield, Michael S., Notarangelo, Luigi D.
প্রকাশিত 2009

Defective B cell tolerance in adenosine deaminase deficiency is corrected by gene therapy

অনুযায়ী Sauer, Aisha V., Morbach, Henner, Brigida, Immacolata, Ng, Yen-Shing, Aiuti, Alessandro, Meffre, Eric
প্রকাশিত 2012

Gene therapy for mucopolysaccharidoses: in vivo and ex vivo approaches

অনুযায়ী Fraldi, Alessandro, Serafini, Marta, Sorrentino, Nicolina Cristina, Gentner, Bernhard, Aiuti, Alessandro, Bernardo, Maria Ester
প্রকাশিত Ital J Pediatr (2018)

Multiparametric Whole Blood Dissection: A one‐shot comprehensive picture of the human hematopoietic system

অনুযায়ী Basso‐Ricci, Luca, Scala, Serena, Milani, Raffaella, Migliavacca, Maddalena, Rovelli, Attilio, Bernardo, Maria Ester, Ciceri, Fabio, Aiuti, Alessandro, Biasco, Luca
প্রকাশিত Cytometry A (2017)

Consensus approach for the management of severe combined immune deficiency caused by adenosine deaminase deficiency

অনুযায়ী Kohn, Donald B., Hershfield, Michael S., Puck, Jennifer M., Aiuti, Alessandro, Blincoe, Annaliesse, Gaspar, H. Bobby, Notarangelo, Luigi D., Grunebaum, Eyal
প্রকাশিত J Allergy Clin Immunol (2018)

Altered intracellular and extracellular signaling leads to impaired T-cell functions in ADA-SCID patients

অনুযায়ী Cassani, Barbara, Mirolo, Massimiliano, Cattaneo, Federica, Benninghoff, Ulrike, Hershfield, Michael, Carlucci, Filippo, Tabucchi, Antonella, Bordignon, Claudio, Roncarolo, Maria Grazia, Aiuti, Alessandro
প্রকাশিত 2008

Role of reduced intensity conditioning in T-cell and B-cell immune reconstitution after HLA-identical bone marrow transplantation in ADA-SCID

অনুযায়ী Cancrini, Caterina, Ferrua, Francesca, Scarselli, Alessia, Brigida, Immacolata, Romiti, Maria Luisa, Barera, Graziano, Finocchi, Andrea, Roncarolo, Maria Grazia, Caniglia, Maurizio, Aiuti, Alessandro
প্রকাশিত 2010

Dendritic cell functional improvement in a preclinical model of lentiviral-mediated gene therapy for Wiskott-Aldrich syndrome

অনুযায়ী Catucci, Marco, Prete, Francesca, Bosticardo, Marita, Castiello, Maria Carmina, Draghici, Elena, Locci, Michela, Roncarolo, Maria Grazia, Aiuti, Alessandro, Benvenuti, Federica, Villa, Anna
প্রকাশিত 2011

Gene Therapy for Adenosine Deaminase Deficiency: A Comprehensive Evaluation of Short- and Medium-Term Safety

অনুযায়ী Cicalese, Maria Pia, Ferrua, Francesca, Castagnaro, Laura, Rolfe, Katie, De Boever, Erika, Reinhardt, Rickey R., Appleby, Jonathan, Roncarolo, Maria Grazia, Aiuti, Alessandro
প্রকাশিত Mol Ther (2018)

Integration profile of retroviral vector in gene therapy treated patients is cell-specific according to gene expression and chromatin conformation of target cell

অনুযায়ী Biasco, Luca, Ambrosi, Alessandro, Pellin, Danilo, Bartholomae, Cynthia, Brigida, Immacolata, Roncarolo, Maria Grazia, Di Serio, Clelia, von Kalle, Christof, Schmidt, Manfred, Aiuti, Alessandro
প্রকাশিত 2011

Efficient Ex Vivo Engineering and Expansion of Highly Purified Human Hematopoietic Stem and Progenitor Cell Populations for Gene Therapy

অনুযায়ী Zonari, Erika, Desantis, Giacomo, Petrillo, Carolina, Boccalatte, Francesco E., Lidonnici, Maria Rosa, Kajaste-Rudnitski, Anna, Aiuti, Alessandro, Ferrari, Giuliana, Naldini, Luigi, Gentner, Bernhard
প্রকাশিত Stem Cell Reports (2017)