Efficient Ex Vivo Engineering and Expansion of Highly Purified Human Hematopoietic Stem and Progenitor Cell Populations for Gene Therapy

Por Zonari, Erika, Desantis, Giacomo, Petrillo, Carolina, Boccalatte, Francesco E., Lidonnici, Maria Rosa, Kajaste-Rudnitski, Anna, Aiuti, Alessandro, Ferrari, Giuliana, Naldini, Luigi, Gentner, Bernhard
Publicado no Stem Cell Reports (2017)

Dual-regulated Lentiviral Vector for Gene Therapy of X-linked Chronic Granulomatosis

Por Chiriaco, Maria, Farinelli, Giada, Capo, Valentina, Zonari, Erika, Scaramuzza, Samantha, Di Matteo, Gigliola, Sergi, Lucia Sergi, Migliavacca, Maddalena, Hernandez, Raisa Jofra, Bombelli, Ferdinando, Giorda, Ezio, Kajaste-Rudnitski, Anna, Trono, Didier, Grez, Manuel, Rossi, Paolo, Finocchi, Andrea, Naldini, Luigi, Gentner, Bernhard, Aiuti, Alessandro
Publicado no Mol Ther (2014)