Hematopoietic Stem Cell Transplantation for Combined Immunodeficiencies, on Behalf of IEWP-EBMT

由 Neven, Benedicte, Ferrua, Francesca
發表在 Front Pediatr (2020)

Gene Therapy for Wiskott-Aldrich Syndrome: History, New Vectors, Future Directions

由 Ferrua, Francesca, Marangoni, Francesco, Aiuti, Alessandro, Roncarolo, Maria Grazia
發表在 J Allergy Clin Immunol (2020)

Role of reduced intensity conditioning in T-cell and B-cell immune reconstitution after HLA-identical bone marrow transplantation in ADA-SCID

由 Cancrini, Caterina, Ferrua, Francesca, Scarselli, Alessia, Brigida, Immacolata, Romiti, Maria Luisa, Barera, Graziano, Finocchi, Andrea, Roncarolo, Maria Grazia, Caniglia, Maurizio, Aiuti, Alessandro
出版 2010

Gene Therapy for Adenosine Deaminase Deficiency: A Comprehensive Evaluation of Short- and Medium-Term Safety

由 Cicalese, Maria Pia, Ferrua, Francesca, Castagnaro, Laura, Rolfe, Katie, De Boever, Erika, Reinhardt, Rickey R., Appleby, Jonathan, Roncarolo, Maria Grazia, Aiuti, Alessandro
發表在 Mol Ther (2018)

A novel genomic inversion in Wiskott-Aldrich–associated autoinflammation

由 Brigida, Immacolata, Scaramuzza, Samantha, Lazarevic, Dejan, Cittaro, Davide, Ferrua, Francesca, Leonardelli, Lorena, Alessio, Maria, Forma, Ornella, Lanzani, Chiara, Viarengo, Gianluca, Ciceri, Fabio, Jankovic, Momcilo, Pesce, Fernando, Aiuti, Alessandro, Cicalese, Maria Pia
發表在 J Allergy Clin Immunol (2016)

B-cell reconstitution after lentiviral vector–mediated gene therapy in patients with Wiskott-Aldrich syndrome

由 Castiello, Maria Carmina, Scaramuzza, Samantha, Pala, Francesca, Ferrua, Francesca, Uva, Paolo, Brigida, Immacolata, Sereni, Lucia, van der Burg, Mirjam, Ottaviano, Giorgio, Albert, Michael H., Grazia Roncarolo, Maria, Naldini, Luigi, Aiuti, Alessandro, Villa, Anna, Bosticardo, Marita
發表在 J Allergy Clin Immunol (2015)

Pioglitazone as a novel therapeutic approach in chronic granulomatous disease

由 Migliavacca, Maddalena, Assanelli, Andrea, Ferrua, Francesca, Cicalese, Maria Pia, Biffi, Alessandra, Frittoli, Marta, Silvani, Paolo, Chidini, Giovanna, Calderini, Edoardo, Mandelli, Anna, Camporesi, Anna, Milani, Raffaella, Farinelli, Giada, Nicoletti, Roberto, Ciceri, Fabio, Aiuti, Alessandro, Bernardo, Maria Ester
發表在 J Allergy Clin Immunol (2016)

First Occurrence of Plasmablastic Lymphoma in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Disease Patient and Review of the Literature

由 Migliavacca, Maddalena, Assanelli, Andrea, Ponzoni, Maurilio, Pajno, Roberta, Barzaghi, Federica, Giglio, Fabio, Ferrua, Francesca, Frittoli, Marta, Brigida, Immacolata, Dionisio, Francesca, Nicoletti, Roberto, Casiraghi, Miriam, Roncarolo, Maria Grazia, Doglioni, Claudio, Peccatori, Jacopo, Ciceri, Fabio, Cicalese, Maria Pia, Aiuti, Alessandro
發表在 Front Immunol (2018)

Urogenital Abnormalities in Adenosine Deaminase Deficiency

由 Pajno, Roberta, Pacillo, Lucia, Recupero, Salvatore, Cicalese, Maria P., Ferrua, Francesca, Barzaghi, Federica, Ricci, Silvia, Marzollo, Antonio, Pecorelli, Silvia, Azzari, Chiara, Finocchi, Andrea, Cancrini, Caterina, Di Matteo, Gigliola, Russo, Gianni, Alfano, Massimo, Lesma, Arianna, Salonia, Andrea, Adams, Stuart, Booth, Claire, Aiuti, Alessandro
發表在 J Clin Immunol (2020)

Premature Senescence and Increased Oxidative Stress in the Thymus of Down Syndrome Patients

由 Marcovecchio, Genni Enza, Ferrua, Francesca, Fontana, Elena, Beretta, Stefano, Genua, Marco, Bortolomai, Ileana, Conti, Anastasia, Montin, Davide, Cascarano, Maria Teresa, Bergante, Sonia, D’Oria, Veronica, Giamberti, Alessandro, Amodio, Donato, Cancrini, Caterina, Carotti, Adriano, Di Micco, Raffaella, Merelli, Ivan, Bosticardo, Marita, Villa, Anna
發表在 Front Immunol (2021)

Thymic Epithelium Abnormalities in DiGeorge and Down Syndrome Patients Contribute to Dysregulation in T Cell Development

由 Marcovecchio, Genni Enza, Bortolomai, Ileana, Ferrua, Francesca, Fontana, Elena, Imberti, Luisa, Conforti, Erika, Amodio, Donato, Bergante, Sonia, Macchiarulo, Giulia, D'Oria, Veronica, Conti, Francesca, Di Cesare, Silvia, Fousteri, Georgia, Carotti, Adriano, Giamberti, Alessandro, Poliani, Pietro Luigi, Notarangelo, Luigi D., Cancrini, Caterina, Villa, Anna, Bosticardo, Marita
發表在 Front Immunol (2019)

Gene Modification and Three‐Dimensional Scaffolds as Novel Tools to Allow the Use of Postnatal Thymic Epithelial Cells for Thymus Regeneration Approaches

由 Bortolomai, Ileana, Sandri, Monica, Draghici, Elena, Fontana, Elena, Campodoni, Elisabetta, Marcovecchio, Genni Enza, Ferrua, Francesca, Perani, Laura, Spinelli, Antonello, Canu, Tamara, Catucci, Marco, Di Tomaso, Tiziano, Sergi Sergi, Lucia, Esposito, Antonio, Lombardo, Angelo, Naldini, Luigi, Tampieri, Anna, Hollander, Georg A., Villa, Anna, Bosticardo, Marita
發表在 Stem Cells Transl Med (2019)

In Vivo Tracking of Human Hematopoiesis Reveals Patterns of Clonal Dynamics during Early and Steady-State Reconstitution Phases

由 Biasco, Luca, Pellin, Danilo, Scala, Serena, Dionisio, Francesca, Basso-Ricci, Luca, Leonardelli, Lorena, Scaramuzza, Samantha, Baricordi, Cristina, Ferrua, Francesca, Cicalese, Maria Pia, Giannelli, Stefania, Neduva, Victor, Dow, David J., Schmidt, Manfred, Von Kalle, Christof, Roncarolo, Maria Grazia, Ciceri, Fabio, Vicard, Paola, Wit, Ernst, Di Serio, Clelia, Naldini, Luigi, Aiuti, Alessandro
發表在 Cell Stem Cell (2016)

Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome

由 Vavassori, Valentina, Mercuri, Elisabetta, Marcovecchio, Genni E, Castiello, Maria C, Schiroli, Giulia, Albano, Luisa, Margulies, Carrie, Buquicchio, Frank, Fontana, Elena, Beretta, Stefano, Merelli, Ivan, Cappelleri, Andrea, Rancoita, Paola MV, Lougaris, Vassilios, Plebani, Alessandro, Kanariou, Maria, Lankester, Arjan, Ferrua, Francesca, Scanziani, Eugenio, Cotta‐Ramusino, Cecilia, Villa, Anna, Naldini, Luigi, Genovese, Pietro
發表在 EMBO Mol Med (2021)

B-cell development and functions and therapeutic options in adenosine deaminase–deficient patients

由 Brigida, Immacolata, Sauer, Aisha V., Ferrua, Francesca, Giannelli, Stefania, Scaramuzza, Samantha, Pistoia, Valentina, Castiello, Maria Carmina, Barendregt, Barbara H., Cicalese, Maria Pia, Casiraghi, Miriam, Brombin, Chiara, Puck, Jennifer, Müller, Klaus, Notarangelo, Lucia Dora, Montin, Davide, van Montfrans, Joris M., Roncarolo, Maria Grazia, Traggiai, Elisabetta, van Dongen, Jacques J. M., van der Burg, Mirjam, Aiuti, Alessandro
發表在 J Allergy Clin Immunol (2014)

Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strim...

由 Tucci, Francesca, Calbi, Valeria, Barzaghi, Federica, Migliavacca, Maddalena, Ferrua, Francesca, Bernardo, Maria Ester, Canarutto, Daniele, Consiglieri, Giulia, Recupero, Salvatore, Calzatini, Francesco, Gabaldo, Michela, Lucano, Caterina, Casiraghi, Miriam, Darin, Silvia, Dionisio, Francesca, Marktel, Sarah, Cestone, Enza, Finazzi, Renato, Mieli‐Vergani, Giorgina, Boeri, Enzo, Appleby, Jonathan, Abd Elaziz, Dalia, Ciceri, Fabio, Aiuti, Alessandro, Cicalese, Maria Pia
發表在 Hepatology (2018)

Lentiviral gene therapy corrects platelet phenotype and function in patients with Wiskott-Aldrich syndrome

由 Sereni, Lucia, Castiello, Maria Carmina, Di Silvestre, Dario, Della Valle, Patrizia, Brombin, Chiara, Ferrua, Francesca, Cicalese, Maria Pia, Pozzi, Loris, Migliavacca, Maddalena, Bernardo, Maria Ester, Pignata, Claudio, Farah, Roula, Notarangelo, Lucia Dora, Marcus, Nufar, Cattaneo, Lorella, Spinelli, Marco, Giannelli, Stefania, Bosticardo, Marita, van Rossem, Koen, D'Angelo, Armando, Aiuti, Alessandro, Mauri, Pierluigi, Villa, Anna
發表在 J Allergy Clin Immunol (2019)

Emapalumab treatment in an ADA-SCID patient with refractory hemophagocytic lymphohistiocytosis- related graft failure and disseminated bacillus Calmette-Guérin infection

由 Tucci, Francesca, Gallo, Vera, Barzaghi, Federica, Ferrua, Francesca, Migliavacca, Maddalena, Calbi, Valeria, Doglio, Matteo, Fratini, Elena Sophia, Karakas, Zeynep, Guner, Sukru, Zambelli, Matilde, Parisi, Cristina, Milani, Raffaella, Gattillo, Salvatore, Mazzi, Benedetta, Oltolini, Chiara, Barbera, Maurizio, Baldoli, Cristina, Cirillo, Daniela Maria, Asnaghi, Veronica, de Min, Cristina, Cicalese, Maria Pia, Ciceri, Fabio, Aiuti, Alessandro, Bernardo, Maria Ester
發表在 Haematologica (2020)

Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency

由 Cicalese, Maria Pia, Ferrua, Francesca, Castagnaro, Laura, Pajno, Roberta, Barzaghi, Federica, Giannelli, Stefania, Dionisio, Francesca, Brigida, Immacolata, Bonopane, Marco, Casiraghi, Miriam, Tabucchi, Antonella, Carlucci, Filippo, Grunebaum, Eyal, Adeli, Mehdi, Bredius, Robbert G., Puck, Jennifer M., Stepensky, Polina, Tezcan, Ilhan, Rolfe, Katie, De Boever, Erika, Reinhardt, Rickey R., Appleby, Jonathan, Ciceri, Fabio, Roncarolo, Maria Grazia, Aiuti, Alessandro
發表在 Blood (2016)

Alterations in the brain adenosine metabolism cause behavioral and neurological impairment in ADA-deficient mice and patients

由 Sauer, Aisha V., Hernandez, Raisa Jofra, Fumagalli, Francesca, Bianchi, Veronica, Poliani, Pietro L., Dallatomasina, Chiara, Riboni, Elisa, Politi, Letterio S., Tabucchi, Antonella, Carlucci, Filippo, Casiraghi, Miriam, Carriglio, Nicola, Cominelli, Manuela, Forcellini, Carlo Alberto, Barzaghi, Federica, Ferrua, Francesca, Minicucci, Fabio, Medaglini, Stefania, Leocani, Letizia, la Marca, Giancarlo, Notarangelo, Lucia D., Azzari, Chiara, Comi, Giancarlo, Baldoli, Cristina, Canale, Sabrina, Sessa, Maria, D’Adamo, Patrizia, Aiuti, Alessandro
發表在 Sci Rep (2017)