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Metabolically Stabilized Double Stranded mRNA Polyplexes

The metabolic instability of mRNA currently limits its utility for gene therapy. Compared to plasmid DNA, mRNA is significantly more susceptible to digestion by RNase in the circulation following systemic dosing. To increase mRNA metabolic stability, we hybridized a complementary reverse mRNA with f...

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Podrobná bibliografie
Vydáno v:Gene Ther
Hlavní autoři: Poliskey, Jacob A., Crowley, Samuel T., Ramanathan, Raghu, White, Christopher W., Mathew, Basil, Rice, Kevin G.
Médium: Artigo
Jazyk:Inglês
Vydáno: 2018
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC6404535/
https://ncbi.nlm.nih.gov/pubmed/30154525
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41434-018-0038-3
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