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RNAi mechanisms in Huntington’s disease therapy: siRNA versus shRNA

Huntington’s Disease (HD) is a genetically dominant trinucleotide repeat disorder resulting from CAG repeats within the Huntingtin (HTT) gene exceeding a normal range (> 36 CAGs). Symptoms of the disease manifest in middle age and include chorea, dystonia, and cognitive decline. Typical latency f...

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Dettagli Bibliografici
Pubblicato in:Transl Neurodegener
Autori principali: Aguiar, Sebastian, van der Gaag, Bram, Cortese, Francesco Albert Bosco
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2017
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5702971/
https://ncbi.nlm.nih.gov/pubmed/29209494
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s40035-017-0101-9
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