A critical base pair in k-turns that confers folding characteristics and correlates with biological function

Por McPhee, Scott A., Huang, Lin, Lilley, David M. J.
Publicado no Nat Commun (2014)

A structural database for k-turn motifs in RNA

Por Schroeder, Kersten T., McPhee, Scott A., Ouellet, Jonathan, Lilley, David M.J.
Publicado em 2010

Structure and folding of a rare, natural kink turn in RNA with an A•A pair at the 2b•2n position

Por Schroeder, Kersten T., Daldrop, Peter, McPhee, Scott A., Lilley, David M.J.
Publicado em 2012

The Structure of Sulfoindocarbocyanine 3 Terminally Attached to dsDNA via a Long, Flexible Tether

Por Urnavicius, Linas, McPhee, Scott A., Lilley, David M.J., Norman, David G.
Publicado em 2012

Transcriptional Regulation of N-acetylaspartate Metabolism in the 5xFAD Model of Alzheimer's Disease: Evidence for Neuron-Glia Communication During Energetic Crisis

Por Zaroff, Samantha, Leone, Paola, McPhee, Scott W. J., Markov, Vladimir, Francis, Jeremy S.
Publicado no Mol Cell Neurosci (2015)

Fluorescent RNA cytosine analogue – an internal probe for detailed structure and dynamics investigations

Por Füchtbauer, Anders Foller, Preus, Søren, Börjesson, Karl, McPhee, Scott A., Lilley, David M. J., Wilhelmsson, L. Marcus
Publicado no Sci Rep (2017)

Prediction of Adeno-Associated Virus Neutralizing Antibody Activity for Clinical Application

Por Wang, Mei, Crosby, Ashley, Hastie, Eric, Samulski, Jade J., McPhee, Scott, Joshua, Grieger, Samulski, R. Jude, Li, Chengwen
Publicado no Gene Ther (2015)

Development of Patient-specific AAV Vectors After Neutralizing Antibody Selection for Enhanced Muscle Gene Transfer

Por Li, Chengwen, Wu, Shuqing, Albright, Blake, Hirsch, Matthew, Li, Wuping, Tseng, Yu-Shan, Agbandje-McKenna, Mavis, McPhee, Scott, Asokan, Aravind, Samulski, R Jude
Publicado no Mol Ther (2016)

Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle

Por Asokan, Aravind, Conway, Julia C, Phillips, Jana L, Li, Chengwen, Hegge, Julia, Sinnott, Rebecca, Yadav, Swati, DiPrimio, Nina, Nam, Hyun-Joo, Agbandje-McKenna, Mavis, McPhee, Scott, Wolff, Jon, Samulski, R Jude
Publicado em 2009

Efficient transduction of vascular smooth muscle cells with a translational AAV2.5 vector: a new perspective for in-stent restenosis gene therapy

Por Lompré, Anne-Marie, Hadri, Lahouaria, Merlet, Elise, Keuylian, Zela, Mougenot, Nathalie, Karakikes, Ioannis, Chen, Jiqiu, Atassi, Fabrice, Marchand, Alexandre, Blaise, Regis, Limon, Isabelle, McPhee, Scott W.J., Samulski, Richard J., Hajjar, Roger J., Lipskaia, Larissa
Publicado em 2013

Long-Term Follow-Up After Gene Therapy for Canavan Disease

Por Leone, Paola, Shera, David, McPhee, Scott W.J., Francis, Jeremy S., Kolodny, Edwin H., Bilaniuk, Larissa T., Wang, Dah-Jyuu, Assadi, Mitra, Goldfarb, Olga, Goldman, H. Warren, Freese, Andrew, Young, Deborah, During, Matthew J., Samulski, R. Jude, Janson, Christopher G.
Publicado em 2012

Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

Por Bowles, Dawn E, McPhee, Scott WJ, Li, Chengwen, Gray, Steven J, Samulski, Jade J, Camp, Angelique S, Li, Juan, Wang, Bing, Monahan, Paul E, Rabinowitz, Joseph E, Grieger, Joshua C, Govindasamy, Lakshmanan, Agbandje-McKenna, Mavis, Xiao, Xiao, Samulski, R Jude
Publicado em 2012

Employing a Gain-of-Function Factor IX Variant R338L to Advance the Efficacy and Safety of Hemophilia B Human Gene Therapy: Preclinical Evaluation Supporting an Ongoing Adeno-Assoc...

Por Monahan, Paul E., Sun, Junjiang, Gui, Tong, Hu, Genlin, Hannah, William B., Wichlan, David G., Wu, Zhijian, Grieger, Joshua C., Li, Chengwen, Suwanmanee, Thipparat, Stafford, Darrel W., Booth, Carmen J., Samulski, Jade J., Kafri, Tal, McPhee, Scott W.J., Samulski, R. Jude
Publicado no Hum Gene Ther (2015)

Dystrophin Immunity in Duchenne’s Muscular Dystrophy

Por Mendell, Jerry R., Campbell, Katherine, Rodino-Klapac, Louise, Sahenk, Zarife, Shilling, Chris, Lewis, Sarah, Bowles, Dawn, Gray, Steven, Li, Chengwen, Galloway, Gloria, Malik, Vinod, Coley, Brian, Clark, K. Reed, Li, Juan, Xiao, Xiao, Samulski, Jade, McPhee, Scott W., Samulski, R. Jude, Walker, Christopher M.
Publicado em 2010

Cardiac I-1c Overexpression With Reengineered AAV Improves Cardiac Function in Swine Ischemic Heart Failure

Por Ishikawa, Kiyotake, Fish, Kenneth M, Tilemann, Lisa, Rapti, Kleopatra, Aguero, Jaume, Santos-Gallego, Carlos G, Lee, Ahyoung, Karakikes, Ioannis, Xie, Chaoqin, Akar, Fadi G, Shimada, Yuichi J, Gwathmey, Judith K, Asokan, Aravind, McPhee, Scott, Samulski, Jade, Samulski, Richard Jude, Sigg, Daniel C, Weber, Thomas, Kranias, Evangelia G, Hajjar, Roger J
Publicado no Mol Ther (2014)