Reply to Letter to the Editor

Por Mendell, Jerry R.
Publicado no Mol Ther (2017)

Duchenne muscular dystrophy: CRISPR/Cas9 treatment

Por Mendell, Jerry R, Rodino-Klapac, Louise R
Publicado no Cell Res (2016)

Casein Kinase 1 alpha associates with the tau-bearing lesions of inclusion body myositis

Por Kannanayakal, Theresa J., Mendell, Jerry R., Kuret, Jeff
Publicado em 2007

The Congenital Muscular Dystrophies: Recent Advances and Molecular Insights

Por Mendell, Jerry R., Boué, Daniel R., Martin, Paul T.
Publicado em 2006

Emerging Drugs for Duchenne Muscular Dystrophy

Por Malik, Vinod, Rodino-Klapac, Louise, Mendell, Jerry R.
Publicado em 2012

Evaluatíon and treatment of myopathies /

Por Griggs, Robert C., Mendell, Jerry R., Miller, Robert G.
Publicado em 1995

Could gene therapy be the future for muscular dystrophy?

Por Haidet, Amanda M, Mendell, Jerry R, Kaspar, Brian K
Publicado em 2010

Molecular Therapeutic Strategies Targeting Duchenne Muscular Dystrophy

Por Mendell, Jerry R., Rodino-Klapac, Louise R., Malik, Vinod
Publicado em 2010

Gene Therapy for Muscular Dystrophy: Moving the Field Forward

Por Al-Zaidy, Samiah, Rodino-Klapac, Louise, Mendell, Jerry R
Publicado no Pediatr Neurol (2014)

Update on the Treatment of Duchenne Muscular Dystrophy

Por Rodino-Klapac, Louise R., Mendell, Jerry R., Sahenk, Zarife
Publicado no Curr Neurol Neurosci Rep (2013)

Aminoglycoside-induced mutation suppression (stop codon readthrough) as a therapeutic strategy for Duchenne muscular dystrophy

Por Malik, Vinod, Rodino-Klapac, Louise R., Viollet, Laurence, Mendell, Jerry R.
Publicado em 2010

MicroRNA-29 overexpression by adeno-associated virus suppresses fibrosis and restores muscle function in combination with micro-dystrophin

Por Heller, Kristin N., Mendell, Joshua T., Mendell, Jerry R., Rodino-Klapac, Louise R.
Publicado no JCI Insight (2017)

A Roadmap to Newborn Screening for Duchenne Muscular Dystrophy

Por Al-Zaidy, Samiah A., Lloyd-Puryear, Michele, Kennedy, Annie, Lopez, Veronica, Mendell, Jerry R.
Publicado no Int J Neonatal Screen (2017)

Follistatin Gene Therapy Improves Ambulation in Becker Muscular Dystrophy

Por Al-Zaidy, Samiah A., Sahenk, Zarife, Rodino-Klapac, Louise R., Kaspar, Brian, Mendell, Jerry R.
Publicado no J Neuromuscul Dis (2015)

Systemic AAV-Mediated β-Sarcoglycan Delivery Targeting Cardiac and Skeletal Muscle Ameliorates Histological and Functional Deficits in LGMD2E Mice

Por Pozsgai, Eric R., Griffin, Danielle A., Heller, Kristin N., Mendell, Jerry R., Rodino-Klapac, Louise R.
Publicado no Mol Ther (2017)

Rapid Direct Sequence Analysis of the Dystrophin Gene

Por Flanigan, Kevin M., Niederhausern, Andrew von, Dunn, Diane M., Alder, Jonathan, Mendell, Jerry R., Weiss, Robert B.
Publicado em 2003

INHIBITION OF MYOSTATIN WITH EMPHASIS ON FOLLISTATIN AS A THERAPY FOR MUSCLE DISEASE

Por RODINO-KLAPAC, LOUISE R., HAIDET, AMANDA M., KOTA, JANAIAH, HANDY, CHALONDA, KASPAR, BRIAN K., MENDELL, JERRY R.
Publicado em 2009

Long-Term Pulmonary Function in Duchenne Muscular Dystrophy: Comparison of Eteplirsen-Treated Patients to Natural History

Por Kinane, T. Bernard, Mayer, Oscar H., Duda, Petra W., Lowes, Linda P., Moody, Stephanie L., Mendell, Jerry R.
Publicado no J Neuromuscul Dis (2018)

Anti-Dystrophin T Cell Responses in Duchenne Muscular Dystrophy: Prevalence and a Glucocorticoid Treatment Effect

Por Flanigan, Kevin M., Campbell, Katie, Viollet, Laurence, Wang, Wei, Gomez, Ana Maria, Walker, Christopher M., Mendell, Jerry R.
Publicado em 2013

Utility of Cystatin C to monitor renal function in Duchenne muscular dystrophy

Por Viollet, Laurence, Gailey, Susan, Thornton, David J., Friedman, Neil R., Flanigan, Kevin M., Mahan, John D., Mendell, Jerry R.
Publicado em 2009