Peptide nucleic acids, morpholinos and related antisense biomolecules

Por Janson, Christopher G., During, Matthew J.
Publicado em 2006

Comparison of Endovascular and Intraventricular Gene Therapy With Adeno-Associated Virus–α-L-Iduronidase for Hurler Disease

Por Janson, Christopher G., Romanova, Liudmila G., Leone, Paola, Nan, Zhenhong, Belur, Lalitha, McIvor, R. Scott, Low, Walter C.
Publicado em 2014

N-acetylaspartate Supports the Energetic Demands of Developmental Myelination via Oligodendroglial Aspartoacylase

Por Francis, Jeremy S., Wojtas, Ireneusz, Markov, Vladimir, Gray, Steven J., McCown, Thomas J., Samulski, R. Jude, Bilaniuk, Larissa T., Wang, Dah-Jyuu, De Vivo, Darryl C., Janson, Christopher G., Leone, Paola
Publicado no Neurobiol Dis (2016)

Long-Term Follow-Up After Gene Therapy for Canavan Disease

Por Leone, Paola, Shera, David, McPhee, Scott W.J., Francis, Jeremy S., Kolodny, Edwin H., Bilaniuk, Larissa T., Wang, Dah-Jyuu, Assadi, Mitra, Goldfarb, Olga, Goldman, H. Warren, Freese, Andrew, Young, Deborah, During, Matthew J., Samulski, R. Jude, Janson, Christopher G.
Publicado em 2012