Transcriptional Regulation of N-acetylaspartate Metabolism in the 5xFAD Model of Alzheimer's Disease: Evidence for Neuron-Glia Communication During Energetic Crisis

מאת Zaroff, Samantha, Leone, Paola, McPhee, Scott W. J., Markov, Vladimir, Francis, Jeremy S.
הוצא לאור ב Mol Cell Neurosci (2015)

Efficient transduction of vascular smooth muscle cells with a translational AAV2.5 vector: a new perspective for in-stent restenosis gene therapy

מאת Lompré, Anne-Marie, Hadri, Lahouaria, Merlet, Elise, Keuylian, Zela, Mougenot, Nathalie, Karakikes, Ioannis, Chen, Jiqiu, Atassi, Fabrice, Marchand, Alexandre, Blaise, Regis, Limon, Isabelle, McPhee, Scott W.J., Samulski, Richard J., Hajjar, Roger J., Lipskaia, Larissa
יצא לאור 2013

Long-Term Follow-Up After Gene Therapy for Canavan Disease

מאת Leone, Paola, Shera, David, McPhee, Scott W.J., Francis, Jeremy S., Kolodny, Edwin H., Bilaniuk, Larissa T., Wang, Dah-Jyuu, Assadi, Mitra, Goldfarb, Olga, Goldman, H. Warren, Freese, Andrew, Young, Deborah, During, Matthew J., Samulski, R. Jude, Janson, Christopher G.
יצא לאור 2012

Employing a Gain-of-Function Factor IX Variant R338L to Advance the Efficacy and Safety of Hemophilia B Human Gene Therapy: Preclinical Evaluation Supporting an Ongoing Adeno-Assoc...

מאת Monahan, Paul E., Sun, Junjiang, Gui, Tong, Hu, Genlin, Hannah, William B., Wichlan, David G., Wu, Zhijian, Grieger, Joshua C., Li, Chengwen, Suwanmanee, Thipparat, Stafford, Darrel W., Booth, Carmen J., Samulski, Jade J., Kafri, Tal, McPhee, Scott W.J., Samulski, R. Jude
הוצא לאור ב Hum Gene Ther (2015)

BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression

מאת Konkle, Barbara A., Walsh, Christopher E., Escobar, Miguel A., Josephson, Neil C., Young, Guy, von Drygalski, Annette, McPhee, Scott W. J., Samulski, R. Jude, Bilic, Ivan, de la Rosa, Maurus, Reipert, Birgit M., Rottensteiner, Hanspeter, Scheiflinger, Friedrich, Chapin, John C., Ewenstein, Bruce, Monahan, Paul E.
הוצא לאור ב Blood (2021)