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Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle

Reengineering the receptor footprints of adeno-associated virus (AAV) isolates may yield variants with improved properties for clinical applications. We generated a panel of synthetic AAV2 vectors by replacing a hexapeptide sequence in a previously identified heparan sulfate receptor footprint with...

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Dettagli Bibliografici
Autori principali: Asokan, Aravind, Conway, Julia C, Phillips, Jana L, Li, Chengwen, Hegge, Julia, Sinnott, Rebecca, Yadav, Swati, DiPrimio, Nina, Nam, Hyun-Joo, Agbandje-McKenna, Mavis, McPhee, Scott, Wolff, Jon, Samulski, R Jude
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2009
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC2912150/
https://ncbi.nlm.nih.gov/pubmed/20037580
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/nbt.1599
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