Lipidomic Evaluation of Feline Neurologic Disease after AAV Gene Therapy

Por Gray-Edwards, Heather L., Jiang, Xuntian, Randle, Ashley N., Taylor, Amanda R., Voss, Taylor L., Johnson, Aime K., McCurdy, Victoria J., Sena-Esteves, Miguel, Ory, Daniel S., Martin, Douglas R.
Publicado no Mol Ther Methods Clin Dev (2017)

High resolution MRI anatomy of the cat brain at 3 Tesla

Por Gray-Edwards, Heather L., Salibi, Nouha, Josephson, Eleanor M., Hudson, Judith A., Cox, Nancy R., Randle, Ashley N., McCurdy, Victoria J., Bradbury, Allison M., Wilson, Diane U., Beyers, Ronald J., Denney, Thomas S., Martin, Douglas R.
Publicado em 2014

Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector

Por Choudhury, Sourav R, Harris, Anne F, Cabral, Damien J, Keeler, Allison M, Sapp, Ellen, Ferreira, Jennifer S, Gray-Edwards, Heather L, Johnson, Jacob A, Johnson, Aime K, Su, Qin, Stoica, Lorelei, DiFiglia, Marian, Aronin, Neil, Martin, Douglas R, Gao, Guangping, Sena-Esteves, Miguel
Publicado no Mol Ther (2016)

AAV-Mediated Gene Delivery in a Feline Model of Sandhoff Disease Corrects Lysosomal Storage in the Central Nervous System

Por Rockwell, Hannah E., McCurdy, Victoria J., Eaton, Samuel C., Wilson, Diane U., Johnson, Aime K., Randle, Ashley N., Bradbury, Allison M., Gray-Edwards, Heather L., Baker, Henry J., Hudson, Judith A., Cox, Nancy R., Sena-Esteves, Miguel, Seyfried, Thomas N., Martin, Douglas R.
Publicado no ASN Neuro (2015)

Sustained normalization of neurological disease after intracranial gene therapy in a feline model**

Por McCurdy, Victoria J., Johnson, Aime K., Gray-Edwards, Heather, Randle, Ashley N., Brunson, Brandon L., Morrison, Nancy E., Salibi, Nouha, Johnson, Jacob A., Hwang, Misako, Beyers, Ronald J., Leroy, Stanley G., Maitland, Stacy, Denney, Thomas S., Cox, Nancy R., Baker, Henry J., Sena-Esteves, Miguel, Martin, Douglas R.
Publicado no Sci Transl Med (2014)

AAV Mediated Gene Delivery Attenuates Neuroinflammation in Feline Sandhoff Disease

Por Bradbury, Allison M, Peterson, Tiffany A, Gross, Amanda L, Wells, Stephen Z, McCurdy, Victoria J, Wolfe, Karen G, Dennis, John C, Brunson, Brandon L, Gray-Edwards, Heather, Randle, Ashley N, Johnson, Aime K, Morrison, Edward E, Cox, Nancy R, Baker, Henry J, Sena-Esteves, Miguel, Martin, Douglas R
Publicado no Neuroscience (2016)

In Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene Therapy

Por Choudhury, Sourav R, Fitzpatrick, Zachary, Harris, Anne F, Maitland, Stacy A, Ferreira, Jennifer S, Zhang, Yuanfan, Ma, Shan, Sharma, Rohit B, Gray-Edwards, Heather L, Johnson, Jacob A, Johnson, Aime K, Alonso, Laura C, Punzo, Claudio, Wagner, Kathryn R, Maguire, Casey A, Kotin, Robert M, Martin, Douglas R, Sena-Esteves, Miguel
Publicado no Mol Ther (2016)

Therapeutic Response in Feline Sandhoff Disease Despite Immunity to Intracranial Gene Therapy

Por Bradbury, Allison M, Cochran, J Nicholas, McCurdy, Victoria J, Johnson, Aime K, Brunson, Brandon L, Gray-Edwards, Heather, Leroy, Stanley G, Hwang, Misako, Randle, Ashley N, Jackson, Laura S, Morrison, Nancy E, Baek, Rena C, Seyfried, Thomas N, Cheng, Seng H, Cox, Nancy R, Baker, Henry J, Cachón-González, M Begona, Cox, Timothy M, Sena-Esteves, Miguel, Martin, Douglas R
Publicado em 2013

Biomarkers for disease progression and AAV therapeutic efficacy in feline Sandhoff disease

Por Bradbury, Allison M, Gray-Edwards, Heather L, Shirley, Jamie L, McCurdy, Victoria J, Colaco, Alexandria N, Randle, Ashley N, Christopherson, Pete W, Bird, Allison C, Johnson, Aime K, Wilson, Diane U, Hudson, Judith A, De Pompa, Nicholas L, Sorjonen, Donald C, Brunson, Brandon L, Jeyakumar, Mylvaganam, Platt, Frances M, Baker, Henry J, Cox, Nancy R, Sena-Esteves, Miguel, Martin, Douglas R
Publicado no Exp Neurol (2014)

Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model

Por Gray-Edwards, Heather L., Regier, Debra S., Shirley, Jamie L., Randle, Ashley N., Salibi, Nouha, Thomas, Sarah E., Latour, Yvonne L., Johnston, Jean, Golas, Gretchen, Maguire, Annie S., Taylor, Amanda R., Sorjonen, Donald C., McCurdy, Victoria J., Christopherson, Peter W., Bradbury, Allison M., Beyers, Ronald J., Johnson, Aime K., Brunson, Brandon L., Cox, Nancy R., Baker, Henry J., Denney, Thomas S., Sena-Esteves, Miguel, Tifft, Cynthia J., Martin, Douglas R.
Publicado no Mol Ther (2017)