Sustained normalization of neurological disease after intracranial gene therapy in a feline model**

Por McCurdy, Victoria J., Johnson, Aime K., Gray-Edwards, Heather, Randle, Ashley N., Brunson, Brandon L., Morrison, Nancy E., Salibi, Nouha, Johnson, Jacob A., Hwang, Misako, Beyers, Ronald J., Leroy, Stanley G., Maitland, Stacy, Denney, Thomas S., Cox, Nancy R., Baker, Henry J., Sena-Esteves, Miguel, Martin, Douglas R.
Publicado no Sci Transl Med (2014)

Direct Intracranial Injection of AAVrh8 Encoding Monkey β-N-Acetylhexosaminidase Causes Neurotoxicity in the Primate Brain

Por Golebiowski, Diane, van der Bom, Imramsjah M.J., Kwon, Churl-Su, Miller, Andrew D., Petrosky, Keiko, Bradbury, Allison M., Maitland, Stacy, Kühn, Anna Luisa, Bishop, Nina, Curran, Elizabeth, Silva, Nilsa, GuhaSarkar, Dwijit, Westmoreland, Susan V., Martin, Douglas R., Gounis, Matthew J., Asaad, Wael F., Sena-Esteves, Miguel
Publicado no Hum Gene Ther (2017)

In Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene Therapy

Por Choudhury, Sourav R, Fitzpatrick, Zachary, Harris, Anne F, Maitland, Stacy A, Ferreira, Jennifer S, Zhang, Yuanfan, Ma, Shan, Sharma, Rohit B, Gray-Edwards, Heather L, Johnson, Jacob A, Johnson, Aime K, Alonso, Laura C, Punzo, Claudio, Wagner, Kathryn R, Maguire, Casey A, Kotin, Robert M, Martin, Douglas R, Sena-Esteves, Miguel
Publicado no Mol Ther (2016)