Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector

Por Choudhury, Sourav R, Harris, Anne F, Cabral, Damien J, Keeler, Allison M, Sapp, Ellen, Ferreira, Jennifer S, Gray-Edwards, Heather L, Johnson, Jacob A, Johnson, Aime K, Su, Qin, Stoica, Lorelei, DiFiglia, Marian, Aronin, Neil, Martin, Douglas R, Gao, Guangping, Sena-Esteves, Miguel
Publicado no Mol Ther (2016)

Sustained normalization of neurological disease after intracranial gene therapy in a feline model**

Por McCurdy, Victoria J., Johnson, Aime K., Gray-Edwards, Heather, Randle, Ashley N., Brunson, Brandon L., Morrison, Nancy E., Salibi, Nouha, Johnson, Jacob A., Hwang, Misako, Beyers, Ronald J., Leroy, Stanley G., Maitland, Stacy, Denney, Thomas S., Cox, Nancy R., Baker, Henry J., Sena-Esteves, Miguel, Martin, Douglas R.
Publicado no Sci Transl Med (2014)

In Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene Therapy

Por Choudhury, Sourav R, Fitzpatrick, Zachary, Harris, Anne F, Maitland, Stacy A, Ferreira, Jennifer S, Zhang, Yuanfan, Ma, Shan, Sharma, Rohit B, Gray-Edwards, Heather L, Johnson, Jacob A, Johnson, Aime K, Alonso, Laura C, Punzo, Claudio, Wagner, Kathryn R, Maguire, Casey A, Kotin, Robert M, Martin, Douglas R, Sena-Esteves, Miguel
Publicado no Mol Ther (2016)