Sustained normalization of neurological disease after intracranial gene therapy in a feline model**

Por McCurdy, Victoria J., Johnson, Aime K., Gray-Edwards, Heather, Randle, Ashley N., Brunson, Brandon L., Morrison, Nancy E., Salibi, Nouha, Johnson, Jacob A., Hwang, Misako, Beyers, Ronald J., Leroy, Stanley G., Maitland, Stacy, Denney, Thomas S., Cox, Nancy R., Baker, Henry J., Sena-Esteves, Miguel, Martin, Douglas R.
Publicado no Sci Transl Med (2014)

AAV Mediated Gene Delivery Attenuates Neuroinflammation in Feline Sandhoff Disease

Por Bradbury, Allison M, Peterson, Tiffany A, Gross, Amanda L, Wells, Stephen Z, McCurdy, Victoria J, Wolfe, Karen G, Dennis, John C, Brunson, Brandon L, Gray-Edwards, Heather, Randle, Ashley N, Johnson, Aime K, Morrison, Edward E, Cox, Nancy R, Baker, Henry J, Sena-Esteves, Miguel, Martin, Douglas R
Publicado no Neuroscience (2016)

Therapeutic Response in Feline Sandhoff Disease Despite Immunity to Intracranial Gene Therapy

Por Bradbury, Allison M, Cochran, J Nicholas, McCurdy, Victoria J, Johnson, Aime K, Brunson, Brandon L, Gray-Edwards, Heather, Leroy, Stanley G, Hwang, Misako, Randle, Ashley N, Jackson, Laura S, Morrison, Nancy E, Baek, Rena C, Seyfried, Thomas N, Cheng, Seng H, Cox, Nancy R, Baker, Henry J, Cachón-González, M Begona, Cox, Timothy M, Sena-Esteves, Miguel, Martin, Douglas R
Publicado em 2013

Biomarkers for disease progression and AAV therapeutic efficacy in feline Sandhoff disease

Por Bradbury, Allison M, Gray-Edwards, Heather L, Shirley, Jamie L, McCurdy, Victoria J, Colaco, Alexandria N, Randle, Ashley N, Christopherson, Pete W, Bird, Allison C, Johnson, Aime K, Wilson, Diane U, Hudson, Judith A, De Pompa, Nicholas L, Sorjonen, Donald C, Brunson, Brandon L, Jeyakumar, Mylvaganam, Platt, Frances M, Baker, Henry J, Cox, Nancy R, Sena-Esteves, Miguel, Martin, Douglas R
Publicado no Exp Neurol (2014)

Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model

Por Gray-Edwards, Heather L., Regier, Debra S., Shirley, Jamie L., Randle, Ashley N., Salibi, Nouha, Thomas, Sarah E., Latour, Yvonne L., Johnston, Jean, Golas, Gretchen, Maguire, Annie S., Taylor, Amanda R., Sorjonen, Donald C., McCurdy, Victoria J., Christopherson, Peter W., Bradbury, Allison M., Beyers, Ronald J., Johnson, Aime K., Brunson, Brandon L., Cox, Nancy R., Baker, Henry J., Denney, Thomas S., Sena-Esteves, Miguel, Tifft, Cynthia J., Martin, Douglas R.
Publicado no Mol Ther (2017)