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Potential of helper-dependent Adenoviral vectors in CRISPR-cas9-mediated lung gene therapy

Since CRISPR/Cas9 was harnessed to edit DNA, the field of gene therapy has witnessed great advances in gene editing. New avenues were created for the treatment of diseases such as Cystic Fibrosis (CF). CF is caused by mutations in the Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) gene....

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Pubblicato in:Cell Biosci
Autori principali: Bandara, Ranmal Avinash, Chen, Ziyan Rachel, Hu, Jim
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2021
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC8305863/
https://ncbi.nlm.nih.gov/pubmed/34301308
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13578-021-00662-w
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