Intravitreal Gene Therapy Reduces Lysosomal Storage in Specific Areas of the CNS in Mucopolysaccharidosis VII Mice

Những quyển sách tương tự

• Chemically modified β-glucuronidase crosses blood–brain barrier and clears neuronal storage in murine mucopolysaccharidosis VII
  Bằng: Grubb, Jeffrey H., et al.
  Được phát hành: (2008)
• Glycosylation-independent targeting enhances enzyme delivery to lysosomes and decreases storage in mucopolysaccharidosis type VII mice
  Bằng: LeBowitz, Jonathan H., et al.
  Được phát hành: (2004)
• Overcoming the blood-brain barrier with high-dose enzyme replacement therapy in murine mucopolysaccharidosis VII
  Bằng: Vogler, Carole, et al.
  Được phát hành: (2005)
• Enzyme therapy in mannose receptor-null mucopolysaccharidosis VII mice defines roles for the mannose 6-phosphate and mannose receptors
  Bằng: Sly, William S., et al.
  Được phát hành: (2006)
• Enzyme replacement therapy for murine mucopolysaccharidosis type VII.
  Bằng: Sands, M S, et al.
  Được phát hành: (1994)