Intravitreal Gene Therapy Reduces Lysosomal Storage in Specific Areas of the CNS in Mucopolysaccharidosis VII Mice

Documenti analoghi

• Chemically modified β-glucuronidase crosses blood–brain barrier and clears neuronal storage in murine mucopolysaccharidosis VII
  di: Grubb, Jeffrey H., et al.
  Pubblicazione: (2008)
• Glycosylation-independent targeting enhances enzyme delivery to lysosomes and decreases storage in mucopolysaccharidosis type VII mice
  di: LeBowitz, Jonathan H., et al.
  Pubblicazione: (2004)
• Overcoming the blood-brain barrier with high-dose enzyme replacement therapy in murine mucopolysaccharidosis VII
  di: Vogler, Carole, et al.
  Pubblicazione: (2005)
• Enzyme therapy in mannose receptor-null mucopolysaccharidosis VII mice defines roles for the mannose 6-phosphate and mannose receptors
  di: Sly, William S., et al.
  Pubblicazione: (2006)
• Enzyme replacement therapy for murine mucopolysaccharidosis type VII.
  di: Sands, M S, et al.
  Pubblicazione: (1994)