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Leveraging Rules of Nonsense-Mediated mRNA Decay for Genome Engineering and Personalized Medicine

Nonsense-mediated mRNA decay (NMD) is a eukaryotic mRNA quality control and regulatory process that plays direct roles in human health and disease. In this Minireview, we discuss how understanding the molecular events that trigger NMD can facilitate strategic targeting of genes via CRISPR/Cas9 techn...

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書誌詳細
出版年:Cell
主要な著者: Popp, Maximilian W., Maquat, Lynne E.
フォーマット: Artigo
言語:Inglês
出版事項: 2016
主題:
オンライン・アクセス:https://ncbi.nlm.nih.gov/pmc/articles/PMC4924582/
https://ncbi.nlm.nih.gov/pubmed/27259145
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.cell.2016.05.053
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