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Leveraging Rules of Nonsense-Mediated mRNA Decay for Genome Engineering and Personalized Medicine

Nonsense-mediated mRNA decay (NMD) is a eukaryotic mRNA quality control and regulatory process that plays direct roles in human health and disease. In this Minireview, we discuss how understanding the molecular events that trigger NMD can facilitate strategic targeting of genes via CRISPR/Cas9 techn...

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Dettagli Bibliografici
Pubblicato in:Cell
Autori principali: Popp, Maximilian W., Maquat, Lynne E.
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4924582/
https://ncbi.nlm.nih.gov/pubmed/27259145
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.cell.2016.05.053
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