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Highly efficient RNA-guided genome editing in human cells via delivery of purified Cas9 ribonucleoproteins

RNA-guided engineered nucleases (RGENs) derived from the prokaryotic adaptive immune system known as CRISPR (clustered, regularly interspaced, short palindromic repeat)/Cas (CRISPR-associated) enable genome editing in human cell lines, animals, and plants, but are limited by off-target effects and u...

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Autors principals: Kim, Sojung, Kim, Daesik, Cho, Seung Woo, Kim, Jungeun, Kim, Jin-Soo
Format: Artigo
Idioma:Inglês
Publicat: Cold Spring Harbor Laboratory Press 2014
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4032847/
https://ncbi.nlm.nih.gov/pubmed/24696461
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1101/gr.171322.113
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