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Complete Genetic Correction of iPS Cells From Duchenne Muscular Dystrophy

Human artificial chromosome (HAC) has several advantages as a gene therapy vector, including stable episomal maintenance that avoids insertional mutations and the ability to carry large gene inserts including the regulatory elements. Induced pluripotent stem (iPS) cells have great potential for gene...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Egile Nagusiak: Kazuki, Yasuhiro, Hiratsuka, Masaharu, Takiguchi, Masato, Osaki, Mitsuhiko, Kajitani, Naoyo, Hoshiya, Hidetoshi, Hiramatsu, Kei, Yoshino, Toko, Kazuki, Kanako, Ishihara, Chie, Takehara, Shoko, Higaki, Katsumi, Nakagawa, Masato, Takahashi, Kazutoshi, Yamanaka, Shinya, Oshimura, Mitsuo
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Nature Publishing Group 2009
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC2839293/
https://ncbi.nlm.nih.gov/pubmed/19997091
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2009.274
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