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Optimized adeno-associated viral vector-mediated striatal DOPA delivery restores sensorimotor function and prevents dyskinesias in a model of advanced Parkinson’s disease

Viral vector-mediated gene transfer utilizing adeno-associated viral vectors has recently entered clinical testing as a novel tool for delivery of therapeutic agents to the brain. Clinical trials in Parkinson’s disease using adeno-associated viral vector-based gene therapy have shown the safety of t...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Egile Nagusiak: Björklund, Tomas, Carlsson, Thomas, Cederfjäll, Erik Ahlm, Carta, Manolo, Kirik, Deniz
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Oxford University Press 2010
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC2822630/
https://ncbi.nlm.nih.gov/pubmed/20129936
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/brain/awp314
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