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Optimized adeno-associated viral vector-mediated striatal DOPA delivery restores sensorimotor function and prevents dyskinesias in a model of advanced Parkinson’s disease

Viral vector-mediated gene transfer utilizing adeno-associated viral vectors has recently entered clinical testing as a novel tool for delivery of therapeutic agents to the brain. Clinical trials in Parkinson’s disease using adeno-associated viral vector-based gene therapy have shown the safety of t...

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Autori principali: Björklund, Tomas, Carlsson, Thomas, Cederfjäll, Erik Ahlm, Carta, Manolo, Kirik, Deniz
Natura: Artigo
Lingua:Inglês
Pubblicazione: Oxford University Press 2010
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC2822630/
https://ncbi.nlm.nih.gov/pubmed/20129936
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/brain/awp314
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