Platelet Gene Therapy by Lentiviral Gene Delivery to Hematopoietic Stem Cells Restores Hemostasis and Induces Humoral Immune Tolerance in FIX(null) Mice

Por Chen, Yingyu, Schroeder, Jocelyn A, Kuether, Erin L, Zhang, Guowei, Shi, Qizhen
Publicado em 2014

Intravascular recovery of VWF and FVIII following intraperitoneal injection and differences from intravenous and subcutaneous injection in mice

Por Shi, Qizhen, Kuether, Erin L., Schroeder, Jocelyn A., Fahs, Scot A., Montgomery, Robert R.
Publicado em 2012

Factor IX ectopically expressed in platelets can be stored in α-granules and corrects the phenotype of hemophilia B mice

Por Zhang, Guowei, Shi, Qizhen, Fahs, Scot A., Kuether, Erin L., Walsh, Christopher E., Montgomery, Robert R.
Publicado em 2010

Targeting FVIII expression to endothelial cells regenerates a releasable pool of FVIII and restores hemostasis in a mouse model of hemophilia A

Por Shi, Qizhen, Fahs, Scot A., Kuether, Erin L., Cooley, Brian C., Weiler, Hartmut, Montgomery, Robert R.
Publicado em 2010

Platelet gene therapy corrects the hemophilic phenotype in immunocompromised hemophilia A mice transplanted with genetically manipulated human cord blood stem cells

Por Shi, Qizhen, Kuether, Erin L., Chen, Yingyu, Schroeder, Jocelyn A., Fahs, Scot A., Montgomery, Robert R.
Publicado em 2014

Correction of Murine Bernard–Soulier Syndrome by Lentivirus-mediated Gene Therapy

Por Kanaji, Sachiko, Kuether, Erin L, Fahs, Scot A, Schroeder, Jocelyn A, Ware, Jerry, Montgomery, Robert R, Shi, Qizhen
Publicado em 2012

Syngeneic transplantation of hematopoietic stem cells that are genetically modified to express factor VIII in platelets restores hemostasis to hemophilia A mice with preexisting FV...

Por Shi, Qizhen, Fahs, Scot A., Wilcox, David A., Kuether, Erin L., Morateck, Patricia A., Mareno, Nicole, Weiler, Hartmut, Montgomery, Robert R.
Publicado em 2008