Polyglutamine-expanded huntingtin exacerbates age-related disruption of nuclear integrity and nucleocytoplasmic transport

door Gasset-Rosa, Fatima, Chillon-Marinas, Carlos, Goginashvili, Alexander, Atwal, Ranjit Singh, Artates, Jonathan W., Tabet, Ricardos, Wheeler, Vanessa C., Bang, Anne G., Cleveland, Don W., Lagier-Tourenne, Clotilde
Gepubliceerd in Neuron (2017)

Exploring the Effect of Sequence Length and Composition on Allele-Selective Inhibition of Human Huntingtin Expression by Single-Stranded Silencing RNAs

door Hu, Jiaxin, Liu, Jing, Yu, Dongbo, Aiba, Yuichiro, Lee, Suheung, Pendergraff, Hannah, Boubaker, Jihane, Artates, Jonathan W., Lagier-Tourenne, Clotilde, Lima, Walt F., Swayze, Eric E., Prakash, Thazha P., Corey, David R.
Gepubliceerd in 2014

Sustained therapeutic reversal of Huntington’s disease by transient repression of huntingtin synthesis

door Kordasiewicz, Holly B., Stanek, Lisa M., Wancewicz, Edward V., Mazur, Curt, McAlonis, Melissa M., Pytel, Kimberly A., Artates, Jonathan W., Weiss, Andreas, Cheng, Seng H., Shihabuddin, Lamya S., Hung, Gene, Bennett, C. Frank, Cleveland, Don W.
Gepubliceerd in 2012

Targeted degradation of sense and antisense C9orf72 RNA foci as therapy for ALS and frontotemporal degeneration

door Lagier-Tourenne, Clotilde, Baughn, Michael, Rigo, Frank, Sun, Shuying, Liu, Patrick, Li, Hai-Ri, Jiang, Jie, Watt, Andrew T., Chun, Seung, Katz, Melanie, Qiu, Jinsong, Sun, Ying, Ling, Shuo-Chien, Zhu, Qiang, Polymenidou, Magdalini, Drenner, Kevin, Artates, Jonathan W., McAlonis-Downes, Melissa, Markmiller, Sebastian, Hutt, Kasey R., Pizzo, Donald P., Cady, Janet, Harms, Matthew B., Baloh, Robert H., Vandenberg, Scott R., Yeo, Gene W., Fu, Xiang-Dong, Bennett, C. Frank, Cleveland, Don W., Ravits, John
Gepubliceerd in 2013