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Effects of mutant huntingtin inactivation on Huntington disease‐related behaviours in the BACHD mouse model

AIMS: Huntington disease (HD) is a fatal neurodegenerative disorder with no disease‐modifying treatments approved so far. Ongoing clinical trials are attempting to reduce huntingtin (HTT) expression in the central nervous system (CNS) using different strategies. Yet, the distribution and timing of H...

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Dettagli Bibliografici
Pubblicato in:Neuropathol Appl Neurobiol
Autori principali: Cheong, Rachel Y., Baldo, Barbara, Sajjad, Muhammad U., Kirik, Deniz, Petersén, Åsa
Natura: Artigo
Lingua:Inglês
Pubblicazione: John Wiley and Sons Inc. 2021
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC8247873/
https://ncbi.nlm.nih.gov/pubmed/33330988
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/nan.12682
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