Biochemical evaluation of intracerebroventricular rhNAGLU-IGF2 enzyme replacement therapy in neonatal mice with Sanfilippo B syndrome

समान संसाधन

• Differential Uptake of NAGLU-IGF2 and Unmodified NAGLU in Cellular Models of Sanfilippo Syndrome Type B
  द्वारा: Prill, Heather, और अन्य
  प्रकाशित: (2019)
• NAGLU mutations underlying Sanfilippo syndrome type B.
  द्वारा: Schmidtchen, A, और अन्य
  प्रकाशित: (1998)
• Behavioral deficits and cholinergic pathway abnormalities in male Sanfilippo B mice
  द्वारा: Kan, Shih-hsin, और अन्य
  प्रकाशित: (2016)
• Clearance of Heparan Sulfate and Attenuation of CNS Pathology by Intracerebroventricular BMN 250 in Sanfilippo Type B Mice
  द्वारा: Aoyagi-Scharber, Mika, और अन्य
  प्रकाशित: (2017)
• A novel mutation in the NAGLU gene associated with Sanfilippo syndrome type B (mucopolysaccharidosis III B)
  द्वारा: Hettiarachchi, Dineshani, और अन्य
  प्रकाशित: (2018)