Lataa...
Platelet-targeted hyperfunctional FIX gene therapy for hemophilia B mice even with preexisting anti-FIX immunity
Gene therapy may lead to a cure for hemophilia B (HB) if it is successful. Data from clinical trials using adeno-associated virus (AAV)–mediated liver-targeted FIX gene therapy are very encouraging. However, this protocol can be applied only to adults who do not have liver disease or anti-AAV antibo...
Tallennettuna:
| Julkaisussa: | Blood Adv |
|---|---|
| Päätekijät: | , , , , , , , |
| Aineistotyyppi: | Artigo |
| Kieli: | Inglês |
| Julkaistu: |
American Society of Hematology
2021
|
| Aiheet: | |
| Linkit: | https://ncbi.nlm.nih.gov/pmc/articles/PMC7948262/ https://ncbi.nlm.nih.gov/pubmed/33646304 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/bloodadvances.2020004071 |
| Tagit: |
Lisää tagi
Ei tageja, Lisää ensimmäinen tagi!
|