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Optimizing Lentiviral Vector Transduction of Hematopoietic Stem Cells for Gene Therapy

Autologous gene therapy using lentiviral vectors (LVs) holds promise for treating monogenetic blood diseases. However, clinical applications can be limited by suboptimal hematopoietic stem cell (HSC) transduction and insufficient quantities of available vector. We recently reported gene therapy for...

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Detalhes bibliográficos
Publicado no:Gene Ther
Main Authors: Jang, Yoonjeong, Kim, Yoon-Sang, Wielgosz, Matthew M., Ferrara, Francesca, Ma, Zhijun, Condori, Jose, Palmer, Lance E., Zhao, Xiwen, Kang, Guolian, Rawlings, David J., Zhou, Sheng, Ryu, Byoung Y.
Formato: Artigo
Idioma:Inglês
Publicado em: 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7606410/
https://ncbi.nlm.nih.gov/pubmed/32341484
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41434-020-0150-z
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