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A Splice Intervention Therapy for Autosomal Recessive Juvenile Parkinson’s Disease Arising from Parkin Mutations

Parkin-type autosomal recessive juvenile-onset Parkinson’s disease is caused by mutations in the PRKN gene and accounts for 50% of all autosomal recessive Parkinsonism cases. Parkin is a neuroprotective protein that has dual functions as an E3 ligase in the ubiquitin–proteasome system and as a trans...

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Détails bibliographiques
Publié dans:Int J Mol Sci
Auteurs principaux: Li, Dunhui, Aung-Htut, May T., Ham, Kristin A., Fletcher, Sue, Wilton, Steve D.
Format: Artigo
Langue:Inglês
Publié: MDPI 2020
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC7582384/
https://ncbi.nlm.nih.gov/pubmed/33019779
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms21197282
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