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Questions Answered and Unanswered by the First CRISPR Editing Study in a Canine Model of Duchenne Muscular Dystrophy

Clustered regularly interspaced short palindromic repeats (CRISPR) editing is being considered as a potential gene repair therapy to treat Duchenne muscular dystrophy, a dystrophin-deficient lethal muscle disease affecting all muscles in the body. A recent preliminary study from the Olson laboratory...

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Dades bibliogràfiques
Publicat a:Hum Gene Ther
Autors principals: Wasala, Nalinda B., Hakim, Chady H., Chen, Shi-Jie, Yang, N. Nora, Duan, Dongsheng
Format: Artigo
Idioma:Inglês
Publicat: Mary Ann Liebert, Inc., publishers 2019
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6534086/
https://ncbi.nlm.nih.gov/pubmed/30648435
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2018.243
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