Cargando...

Questions Answered and Unanswered by the First CRISPR Editing Study in a Canine Model of Duchenne Muscular Dystrophy

Clustered regularly interspaced short palindromic repeats (CRISPR) editing is being considered as a potential gene repair therapy to treat Duchenne muscular dystrophy, a dystrophin-deficient lethal muscle disease affecting all muscles in the body. A recent preliminary study from the Olson laboratory...

Descripción completa

Guardado en:
Detalles Bibliográficos
Publicado en:Hum Gene Ther
Autores principales: Wasala, Nalinda B., Hakim, Chady H., Chen, Shi-Jie, Yang, N. Nora, Duan, Dongsheng
Formato: Artigo
Lenguaje:Inglês
Publicado: Mary Ann Liebert, Inc., publishers 2019
Materias:
Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6534086/
https://ncbi.nlm.nih.gov/pubmed/30648435
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2018.243
Etiquetas: Agregar Etiqueta
Sin Etiquetas, Sea el primero en etiquetar este registro!