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Acid ceramidase inhibition ameliorates α-synuclein accumulation upon loss of GBA1 function

GBA1 encodes the lysosomal enzyme β-glucocerebrosidase (GCase) which converts glucosylceramide into ceramide and glucose. Mutations in GBA1 lead to Gaucher’s disease and are a major risk factor for Parkinson’s disease (PD) and Dementia with Lewy bodies (DLB), synucleinopathies characterized by accum...

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Pubblicato in:Hum Mol Genet
Autori principali: Kim, Myung Jong, Jeon, Sohee, Burbulla, Lena F, Krainc, Dimitri
Natura: Artigo
Lingua:Inglês
Pubblicazione: Oxford University Press 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6251682/
https://ncbi.nlm.nih.gov/pubmed/29579237
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddy105
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