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Progranulin-mediated deficiency of cathepsin D results in FTD and NCL-like phenotypes in neurons derived from FTD patients

Frontotemporal dementia (FTD) encompasses a group of neurodegenerative disorders characterized by cognitive and behavioral impairments. Heterozygous mutations in progranulin (PGRN) cause familial FTD and result in decreased PGRN expression, while homozygous mutations result in complete loss of PGRN...

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Detalles Bibliográficos
Publicado en:Hum Mol Genet
Main Authors: Valdez, Clarissa, Wong, Yvette C, Schwake, Michael, Bu, Guojun, Wszolek, Zbigniew K, Krainc, Dimitri
Formato: Artigo
Idioma:Inglês
Publicado: Oxford University Press 2017
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC5886207/
https://ncbi.nlm.nih.gov/pubmed/29036611
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddx364
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