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Progranulin-mediated deficiency of cathepsin D results in FTD and NCL-like phenotypes in neurons derived from FTD patients

Frontotemporal dementia (FTD) encompasses a group of neurodegenerative disorders characterized by cognitive and behavioral impairments. Heterozygous mutations in progranulin (PGRN) cause familial FTD and result in decreased PGRN expression, while homozygous mutations result in complete loss of PGRN...

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Detalhes bibliográficos
Publicado no:Hum Mol Genet
Main Authors: Valdez, Clarissa, Wong, Yvette C, Schwake, Michael, Bu, Guojun, Wszolek, Zbigniew K, Krainc, Dimitri
Formato: Artigo
Idioma:Inglês
Publicado em: Oxford University Press 2017
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5886207/
https://ncbi.nlm.nih.gov/pubmed/29036611
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddx364
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