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An intronic mutation in Chd7 creates a cryptic splice site, causing aberrant splicing in a mouse model of CHARGE syndrome

Alternate splicing is a critical regulator of gene expression in eukaryotes, however genetic mutations can cause erroneous splicing and disease. Most recorded splicing disorders are caused by mutations of splice donor/acceptor sites, however intronic mutations can affect splicing. Clinical exome ana...

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Vydáno v:Sci Rep
Hlavní autoři: Ogier, Jacqueline M., Arhatari, Benedicta D., Carpinelli, Marina R., McColl, Bradley K., Wilson, Michael A., Burt, Rachel A.
Médium: Artigo
Jazyk:Inglês
Vydáno: Nature Publishing Group UK 2018
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC5882948/
https://ncbi.nlm.nih.gov/pubmed/29615807
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41598-018-23856-8
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