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Motor Neuron Gene Therapy: Lessons from Spinal Muscular Atrophy for Amyotrophic Lateral Sclerosis

Spinal muscular atrophy (SMA) and amyotrophic lateral sclerosis (ALS) are severe nervous system diseases characterized by the degeneration of lower motor neurons. They share a number of additional pathological, cellular, and genetic parallels suggesting that mechanistic and clinical insights into on...

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Detalles Bibliográficos
Publicado en:Front Mol Neurosci
Autores principales: Tosolini, Andrew P., Sleigh, James N.
Formato: Artigo
Lenguaje:Inglês
Publicado: Frontiers Media S.A. 2017
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC5725447/
https://ncbi.nlm.nih.gov/pubmed/29270111
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fnmol.2017.00405
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