A Preclinical Study in Rhesus Macaques for Cystic Fibrosis to Assess Gene Transfer and Transduction by AAV1 and AAV5 with a Dual-Luciferase Reporter System

Cystic fibrosis (CF) is an autosomal recessive disease that is potentially treatable by gene therapy. Since the identification of the gene encoding CF transmembrane conductance regulator, a number of preclinical and clinical trials have been conducted using the first generation of adeno-associated v...

Descrizione completa

Salvato in:
Dettagli Bibliografici
Pubblicato in:Hum Gene Ther Clin Dev
Autori principali: Guggino, William B., Benson, Janet, Seagrave, JeanClare, Yan, Ziying, Engelhardt, John, Gao, Guangping, Conlon, Thomas J., Cebotaru, Liudmila
Natura: Artigo
Lingua:Inglês
Pubblicazione: Mary Ann Liebert, Inc. 2017
Soggetti:
Special Focus: Preclinical Studies in Large Animals
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5655841/
https://ncbi.nlm.nih.gov/pubmed/28726496
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/humc.2017.067
Tags: Aggiungi Tag
Nessun Tag, puoi essere il primo ad aggiungerne! !

Documenti analoghi