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Full deacylation of polyethylenimine dramatically boosts its gene delivery efficiency and specificity to mouse lung

High-molecular-mass polyethylenimines (PEIs) are widely used vectors for nucleic acid delivery. We found that removal of the residual N-acyl moieties from commercial linear 25-kDa PEI enhanced its plasmid DNA delivery efficiency 21 times in vitro, as well as 10,000 times in mice with a concomitant 1...

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Autores principales: Thomas, Mini, Lu, James J., Ge, Qing, Zhang, Chengcheng, Chen, Jianzhu, Klibanov, Alexander M.
Formato: Artigo
Lenguaje:Inglês
Publicado: National Academy of Sciences 2005
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC556302/
https://ncbi.nlm.nih.gov/pubmed/15824322
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.0502067102
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