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A 5′ Noncoding Exon Containing Engineered Intron Enhances Transgene Expression from Recombinant AAV Vectors in vivo

We previously developed a mini-intronic plasmid (MIP) expression system in which the essential bacterial elements for plasmid replication and selection are placed within an engineered intron contained within a universal 5′ UTR noncoding exon. Like minicircle DNA plasmids (devoid of bacterial backbon...

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Detalhes bibliográficos
Publicado no:Hum Gene Ther
Main Authors: Lu, Jiamiao, Williams, James A., Luke, Jeremy, Zhang, Feijie, Chu, Kirk, Kay, Mark A.
Formato: Artigo
Idioma:Inglês
Publicado em: Mary Ann Liebert, Inc. 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5278795/
https://ncbi.nlm.nih.gov/pubmed/27903072
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2016.140
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