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In Vivo Delivery Systems for Therapeutic Genome Editing

Therapeutic genome editing technology has been widely used as a powerful tool for directly correcting genetic mutations in target pathological tissues and cells to cure of diseases. The modification of specific genomic sequences can be achieved by utilizing programmable nucleases, such as Meganuclea...

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Dettagli Bibliografici
Pubblicato in:Int J Mol Sci
Autori principali: Wang, Luyao, Li, Fangfei, Dang, Lei, Liang, Chao, Wang, Chao, He, Bing, Liu, Jin, Li, Defang, Wu, Xiaohao, Xu, Xuegong, Lu, Aiping, Zhang, Ge
Natura: Artigo
Lingua:Inglês
Pubblicazione: MDPI 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4881452/
https://ncbi.nlm.nih.gov/pubmed/27128905
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms17050626
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