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In Vivo Delivery Systems for Therapeutic Genome Editing
Therapeutic genome editing technology has been widely used as a powerful tool for directly correcting genetic mutations in target pathological tissues and cells to cure of diseases. The modification of specific genomic sequences can be achieved by utilizing programmable nucleases, such as Meganuclea...
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| Publicado en: | Int J Mol Sci |
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| Autores principales: | , , , , , , , , , , , |
| Formato: | Artigo |
| Lenguaje: | Inglês |
| Publicado: |
MDPI
2016
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| Materias: | |
| Acceso en línea: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4881452/ https://ncbi.nlm.nih.gov/pubmed/27128905 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms17050626 |
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