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Photoreceptor-targeted gene delivery using intravitreally administered AAV vectors in dogs
Delivery of therapeutic transgenes to retinal photoreceptors using adeno-associated virus (AAV) vectors has traditionally required subretinal injection. Recently, photoreceptor transduction efficiency following intravitreal injection (IVT) has improved in rodent models through use of capsid-mutant A...
Kaydedildi:
| Yayımlandı: | Gene Ther |
|---|---|
| Asıl Yazarlar: | , , , , , , , |
| Materyal Türü: | Artigo |
| Dil: | Inglês |
| Baskı/Yayın Bilgisi: |
2015
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| Konular: | |
| Online Erişim: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4840844/ https://ncbi.nlm.nih.gov/pubmed/26467396 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/gt.2015.96 |
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