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CRISPR/Cas9-mediated GJA8 knockout in rabbits recapitulates human congenital cataracts

Cataracts are the leading cause of vision loss in the world, although surgical treatment can restore vision in cataract patients. Until now, there have been no adequate animal models for in vivo studies of artificial lens safety and drug interactions. Genetic studies have demonstrated that GJA8 is i...

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Dettagli Bibliografici
Pubblicato in:Sci Rep
Autori principali: Yuan, Lin, Sui, Tingting, Chen, Mao, Deng, Jichao, Huang, Yongye, Zeng, Jian, Lv, Qingyan, Song, Yuning, Li, Zhanjun, Lai, Liangxue
Natura: Artigo
Lingua:Inglês
Pubblicazione: Nature Publishing Group 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4766569/
https://ncbi.nlm.nih.gov/pubmed/26912477
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/srep22024
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