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Disparate Mutations Confer Therapeutic Gain of Hsp104 Function

Hsp104, a protein disaggregase from yeast, can be engineered and potentiated to counter TDP-43, FUS, or α-synuclein misfolding and toxicity implicated in neurodegenerative disease. Here, we reveal that extraordinarily disparate mutations potentiate Hsp104. Remarkably, diverse single missense mutatio...

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Publicat a:ACS Chem Biol
Autors principals: Jackrel, Meredith E., Yee, Keolamau, Tariq, Amber, Chen, Annie I., Shorter, James
Format: Artigo
Idioma:Inglês
Publicat: 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4684741/
https://ncbi.nlm.nih.gov/pubmed/26441009
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1021/acschembio.5b00765
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