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Antisense Oligo-Mediated Multiple Exon Skipping in a Dog Model of Duchenne Muscular Dystrophy

Exon skipping is currently one of the most promising molecular therapies for Duchenne muscular dystrophy (DMD). We have recently developed multiple exon skipping targeting exons 6 and 8 in dystrophin mRNA of canine X-linked muscular dystrophy (CXMD), an animal model of DMD, which exhibits severe dys...

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Bibliografski detalji
Izdano u:Methods Mol Biol
Glavni autori: Yokota, Toshifumi, Hoffman, Eric, Takeda, Shin’ichi
Format: Artigo
Jezik:Inglês
Izdano: 2011
Teme:
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC4491489/
https://ncbi.nlm.nih.gov/pubmed/21194037
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/978-1-61737-982-6_20
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