ロード中...
Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD), the most common lethal genetic disorder, is caused by mutations in the dystrophin (DMD) gene. Exon skipping is a therapeutic approach that uses antisense oligonucleotides (AOs) to modulate splicing and restore the reading frame, leading to truncated, yet functional...
保存先:
| 出版年: | Mol Ther |
|---|---|
| 主要な著者: | , , , , , , , , , , , , , , , , , |
| フォーマット: | Artigo |
| 言語: | Inglês |
| 出版事項: |
American Society of Gene & Cell Therapy
2017
|
| 主題: | |
| オンライン・アクセス: | https://ncbi.nlm.nih.gov/pmc/articles/PMC5675502/ https://ncbi.nlm.nih.gov/pubmed/28865998 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymthe.2017.07.014 |
| タグ: |
タグ追加
タグなし, このレコードへの初めてのタグを付けませんか!
|